2023 | Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A | Mahlangu, Johnny; Kaczmarek, Radoslaw; von Drygalski, Annette; Shapiro, Susan; SHENG-CHIEH CHOU ; Ozelo, Margareth C; Kenet, Gili; Peyvandi, Flora; Wang, Michael; Madan, Bella; Key, Nigel S; Laffan, Michael; Dunn, Amy L; Mason, Jane; Quon, Doris V; Symington, Emily; Leavitt, Andrew D; Oldenburg, Johannes; Chambost, Hervé; Reding, Mark T; Jayaram, Kala; Yu, Hua; Mahajan, Reena; Chavele, Konstantia-Maria; Reddy, Divya B; Henshaw, Joshua; Robinson, Tara M; Wong, Wing Yen; Pipe, Steven W | The New England journal of medicine | 46 | 24 | |