2017 | Clinical evaluation of glycoPEGylated recombinant FVIII: Efficacy and safety in severe haemophilia A | Giangrande, Paul; Andreeva, Tatiana; Chowdary, Pratima; Ehrenforth, Silke; Hanabusa, Hideji; Leebeek, Frank W G; Lentz, Steven R; Nemes, Laszlo; Poulsen, Lone Hvitfeldt; Santagostino, Elena; You, Chur Woo; Clausen, Wan Hui Ong; Jönsson, Peter G; MING-CHING SHEN ; Oldenburg, Johannes; WOEI TSAY | Thrombosis and haemostasis | 88 | 87 | |
2023 | Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A | Mahlangu, Johnny; Kaczmarek, Radoslaw; von Drygalski, Annette; Shapiro, Susan; SHENG-CHIEH CHOU ; Ozelo, Margareth C; Kenet, Gili; Peyvandi, Flora; Wang, Michael; Madan, Bella; Key, Nigel S; Laffan, Michael; Dunn, Amy L; Mason, Jane; Quon, Doris V; Symington, Emily; Leavitt, Andrew D; Oldenburg, Johannes; Chambost, Hervé; Reding, Mark T; Jayaram, Kala; Yu, Hua; Mahajan, Reena; Chavele, Konstantia-Maria; Reddy, Divya B; Henshaw, Joshua; Robinson, Tara M; Wong, Wing Yen; Pipe, Steven W | The New England journal of medicine | 46 | 24 | |