2023 | Characteristics of Patients with Hereditary Transthyretin Amyloidosis-Polyneuropathy (ATTRv-PN) in NEURO-TTRansform, an Open-label Phase 3 Study of Eplontersen | Coelho, Teresa; Waddington Cruz, Márcia; CHI-CHAO CHAO ; Parman, Yeşim; Wixner, Jonas; Weiler, Markus; Barroso, Fabio A; Dasgupta, Noel R; Jung, Shiangtung W; Schneider, Eugene; Viney, Nicholas J; Dyck, P James B; Ando, Yukio; Gillmore, Julian D; Khella, Sami; Gertz, Morie A; Obici, Laura; Berk, John L | Neurology and therapy | 14 | 12 | |
2023 | Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy | Obici, Laura; Ajroud-Driss, Senda; Lin, Kon-Ping; Berk, John L; Gillmore, Julian D; Kale, Parag; Koike, Haruki; Danese, David; Aldinc, Emre; Chen, Chongshu; Vest, John; Adams, David; MING-JEN LEE ; HSUEH-WEN HSUEH ; LI-KAI TSAI ; JEN-JEN SU ; Chou, Hsi-Chieh; CHI-CHAO CHAO ; SUNG-TSANG HSIEH | Neurology and therapy | 7 | 1 | |