公開日期 | 標題 | 作者 | 來源出版物 | scopus | WOS | 全文 |
2015 | An Update on Gene Therapy for the Treatment of Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency | Hwu, Wuh-Liang; Muramatsu, Shin-Ichi; Lee, Ni-Chung; Chien, Yin-Hsiu; Tseng, Sheng-Hong; Tzen, Kai-Yuan; Snyder, Richard O.; Byrne, Barry J.; Tai, Chun-Hwei; Wu, Ruey-Meei | Mol. Ther. | | | |
2012 | Gene Therapy for Aromatic L-Amino Acid Decarboxylase Deficiency | Hwu, Wuh-Liang; Muramatsu, Shin-ichi; Tseng, Sheng-Hong; Tzen, Kai-Yuan; Lee, Ni-Chung; Chien, Yin-Hsiu; Snyder, Richard O.; Byrne, Barry J.; Tai, Chun-Hwei; Wu, Ruey-Meei | Neurosurgery | 4 | 4 | |
2013 | Gene Therapy for Aromatic L-Amino Acid Decarboxylase Deficiency: Report of Treatment for 8 Patients | Hwu, Wuh-Liang; Muramatsu, Shin-ichi; Tseng, Sheng-Hong; Tzen, Kai-Yuan; Lee, Ni-Chung; Chien, Yin-Hsiu; Snyder, Richard O.; Byrne, Barry; Tai, Chun-Hwei; Wu, Ruey-Meei | Mol. Ther. | | | |
2021 | Gene therapy in the putamen for curing AADC deficiency and Parkinson's disease | WUH-LIANG HWU ; Kiening, Karl; Anselm, Irina; Compton, David R; Nakajima, Takeshi; Opladen, Thomas; Pearl, Phillip L; Roubertie, Agathe; Roujeau, Thomas; Muramatsu, Shin-Ichi | EMBO Molecular Medicine | 17 | 17 | |
2022 | Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency | Tai, Chun-Hwei; NI-CHUNG LEE ; YIN-HSIU CHIEN ; Byrne, Barry J; Muramatsu, Shin-Ichi; SHENG-HONG TSENG ; WUH-LIANG HWU | Molecular therapy : the journal of the American Society of Gene Therapy | 48 | 44 | |
2022 | Reduced Immunogenicity of Intraparenchymal Delivery of Adeno-Associated Virus Serotype 2 Vectors: Brief Overview | WUH-LIANG HWU ; Muramatsu, Shin-Ichi; Gidoni-Ben-Zeev, Bruria | Current gene therapy | 2 | 2 | |