Plain language summary of 4-year results of the GENEr8-1 clinical trial of valoctocogene roxaparvovec gene therapy for hemophilia A

Journal

Future Rare Diseases

Journal Volume

5

Journal Issue

1

Start Page

Article number 2522071

ISSN

2399-5270

Date Issued

2025-07-07

Author(s)

Madan, Bella

Ozelo, Margareth C.

Kenet, Gili

Dashiell-Aje, Ebony

Robinson, Tara M.

Mahlangu, Johnny

Recht, Michael

Careta, Francisco P.

Ruiz, Andres

Fletcher, Simon

Goshen, Dor

DOI

URI

Publisher

Informa UK Limited

Type

journal article