Early initiation of high-dose oral ambroxol in combination with enzyme replacement therapy in a neuropathic Gaucher infant
Journal
Blood Cells, Molecules, and Diseases
Journal Volume
81
Pages
102402
Date Issued
2020
Author(s)
SDGs
Other Subjects
ambroxol; imiglucerase; ambroxol; clinical article; combination drug therapy; drug megadose; enzyme replacement; female; Gaucher disease; human; infant; Letter; newborn; priority journal; case report; combination drug therapy; enzyme replacement; Gaucher disease; procedures; time to treatment; treatment outcome; Ambroxol; Drug Therapy, Combination; Enzyme Replacement Therapy; Gaucher Disease; Humans; Infant; Time-to-Treatment; Treatment Outcome
Publisher
Academic Press Inc.
Type
letter