Efficacy, safety and cost of emicizumab prophylaxis in haemophilia A patients with inhibitors: A nationwide observational study in Taiwan
Journal
Haemophilia : the official journal of the World Federation of Hemophilia
Journal Volume
29
Journal Issue
6
Date Issued
2023-11
Author(s)
Chiou, Shyh-Shin
Lin, Pei-Chin
Chen, Yeu-Chin
Lin, Hsuan-Yu
Lee, Yang-Cheng
Huang, Cih-En
Weng, Te-Fu
Huang, Ting-Huan
Chung, Chih-Yuan
Chen, Jiann-Shiuh
Chen, Shu-Huey
Cheng, Shin-Nan
Hsiao, Chih-Cheng
Huang, Yen-Min
Chen, Shih-Hsiang
Yu, Yuan-Bin
Lin, Shih-Chiang
Lin, Ching-Yeh
Peng, Ching-Tien
Wang, Jiaan-Der
Abstract
Emicizumab mimicking the cofactor function of activated factor VIII (FVIII) restores haemostasis.
Subjects
cost; efficacy; emicizumab; factor VIII inhibitors; haemophilia A; safety
Type
journal article
