臺大醫院;臺大醫院-小兒部;臺大醫院-外科部;臺大醫院-核子醫學部;臺大醫院-神經部;臺大醫院-基因醫學部;Hwu, Wuh-LiangWuh-LiangHwuMuramatsu, Shin-ichiShin-ichiMuramatsuTseng, Sheng-HongSheng-HongTsengTzen, Kai-YuanKai-YuanTzenLee, Ni-ChungNi-ChungLeeChien, Yin-HsiuYin-HsiuChienSnyder, Richard O.Richard O.SnyderByrne, BarryBarryByrneTai, Chun-HweiChun-HweiTaiWu, Ruey-MeeiRuey-MeeiWu2014-02-142018-07-112014-02-142018-07-112013http://ntur.lib.ntu.edu.tw//handle/246246/259870Gene Therapy for Aromatic L-Amino Acid Decarboxylase Deficiency: Report of Treatment for 8 Patients