Issue Date | Title | Author(s) | Source | scopus | WOS | Fulltext/Archive link |
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2007 | Treatment of Niemann-Pick disease type C in two children with miglustat: Initial responses and maintenance of effects over 1 year. | Chien, YH; Lee, NC; Tsai, LK; Huang, AC; Peng, SF; Chen, SJ; Hwu, WL | J Inherit Metab Dis |